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Better Technology.
Better Delivery.

Developing a new generation of disease-modifying therapies.

Who We Are

Driven by our proprietary Enhanced Delivery Oligonucleotide (EDO) platform, we are creating a pipeline of disease-modifying therapeutics with the potential to safely and effectively target the root cause of serious genetic neuromuscular and neurological disorders.

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  • Our Pioneering Science

    Creating the new generation of genetic therapies

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  • Our Pipeline

    Advancing transformative therapies to treat neuromuscular and neurological disorders

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  • Our Community

    Committed to changing the treatment of people living with neuromuscular and neurological disorders​

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