Who We Are
Driven by our proprietary Enhanced Delivery Oligonucleotide (EDO) platform, we are creating a pipeline of disease-modifying therapeutics with the potential to safely and effectively target the root cause of serious genetic neuromuscular and neurological disorders.
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Our Pipeline
Advancing transformative therapies to treat neuromuscular and neurological disorders
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Our Community
Committed to changing the lives of people living with neuromuscular and neurological disorders
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