Results From The CONNECT1-EDO51 Phase 2 Study Of PGN-EDO51 In People With Duchenne Muscular Dystrophy Amenable To Exon 51 Skipping
Results from 15 mg/kg Single Dose PGN-EDODM1 Cohort of FREEDOM-DM1- a Phase 1 Study in People with Myotonic Dystrophy 1 (DM1)